case_study
    2019

    Senolytics in idiopathic pulmonary fibrosis: Results from a first-in-human, open-label, pilot study

    Justice JN, Nambiar AM, Tchkonia T, LeBrasseur NK

    Published in EBioMedicine

    Methodology

    Two-centre open-label pilot of intermittent dasatinib 100 mg/day plus quercetin 1250 mg/day, three days per week for three weeks, in idiopathic pulmonary fibrosis

    Key Findings

    Retention was 100% and physical function measures (6-minute walk distance, gait speed, chair stands) improved significantly; adverse events were mostly mild to moderate.

    Conclusions

    Senolytic therapy was feasible in a senescence-associated disease and improved physical function measures.

    Limitations

    Open-label, uncontrolled, tiny sample, functional outcomes vulnerable to placebo and learning effects; quercetin not tested alone.

    Supplements Studied

    Quercetin
    Compound

    Physical function evaluated as 6-min walk distance, 4-m gait speed, and chair-stands time was significantly and clinically-mean

    Outcomes Measured

    Physical function evaluated as 6-min walk distance, 4-m gait speed, and chair-stands time was significantly and clinically-mean

    Study Details

    Year:2019
    Sample Size:14
    Duration:3 weeks
    Quality Score:5/10

    Disclosures

    Funding

    NIH and foundations

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